Casgevy (exagamglogene autotemcel)
pCPA File Number:
22969
Negotiation Status:
Active Negotiation
Indication(s):
Transfusion-dependent β-thalassemia
Sponsor/Manufacturer:
Vertex Pharmaceuticals (Canada) Incorporated
CDA-AMC Project Number:
SG0831-000
pCPA Engagement Letter Issued:
Negotiation Process Concluded:
Not Applicable